Spark Therapeutics
About Company
Unlocking the potential of gene therapy, sparking change.
Spark Therapeutics is a fully integrated company based in Philadelphia, PA, with a mission to unlock the power of gene therapy to accelerate healthcare transformation. The company combines its proprietary adeno-associated viral (AAV) gene therapy platform with excellence in R&D, manufacturing, and commercial operations to develop medicines for patients with inherited diseases, including inherited retinal diseases (IRDs), liver-directed diseases such as hemophilia, and neurodegenerative diseases. Spark Therapeutics has announced the development of a Gene Therapy Innovation Center in West Philadelphia, which aims to bring together the greatest minds in gene therapy and serve as a flagship center of excellence for gene therapy manufacturing globally. The company’s commitment to corporate social responsibility, environmental sustainability, ethics, and patient safety is evident through its various initiatives. Spark Therapeutics also collaborates with other organizations for the use of proprietary delivery technology for CNS disorders. For more information, visit [www.sparktx.com](https://www.sparktx.com).